Defining and estimating effects in cluster randomized trials: a methods comparison

DOI10.1002/SIM.9813MaRDI QIDQ6626873zbMATH OpenFDO

Authors Alejandra Benitez, Maya Petersen, Mark J. Van der Laan, Nicole Santos, Elizabeth Butrick, Dilys Walker, Rakesh Ghosh, Phelgona Otieno, Peter Waiswa, Laura Balzer

Publication date 29 October 2024

Published in Statistics in Medicine (Search for Journal in Brave)

Copyright license Creative Commons Attribution 4.0 International

Full work available at URL https://doi.org/10.1002/SIM.9813

zbMATH Keywords

cluster randomized trialsclustered datadata-adaptive adjustmentgroup randomized trialshierarchical datatargeted maximum likelihood estimation

Mathematics Subject Classification ID

Applications of statistics to biology and medical sciences; meta analysis (62P10)

Cites work

• Applied longitudinal analysis.
• Causality. Models, reasoning, and inference
• Comment on J. Neyman and causal inference in experiments and observational studies: On the application of probability theory to agricultural experiments. Essay on principles. Section 9 [Ann. Agric. Sci. 10 (1923), 1--51]
• Effect of breastfeeding on gastrointestinal infection in infants: a targeted maximum likelihood approach for clustered longitudinal data
• Empirical efficiency maximization: improved locally efficient covariate adjustment in randomized experiments and survival analysis
• Improving precision and power in randomized trials for COVID‐19 treatments using covariate adjustment, for binary, ordinal, and time‐to‐event outcomes
• Inference on the marginal distribution of clustered data with informative cluster size
• Locally efficient estimation of marginal treatment effects when outcomes are correlated: is the prize worth the chase?
• Longitudinal data analysis using generalized linear models
• Model-Assisted Analyses of Cluster-Randomized Experiments
• Simple, efficient estimators of treatment effects in randomized trials using generalized linear models to leverage baseline variables
• Small-sample adjustments for Wald-type tests using sandwich estimators
• The essential role of pair matching in cluster-randomized experiments, with application to the Mexican Universal Health Insurance evaluation

Cited in

(5)

• Cluster-level analyses to estimate a risk difference in a cluster randomized trial with confounding individual-level covariates: a simulation study
• Model-robust standardization in cluster-randomized trials
• Handling incomplete outcomes and covariates in cluster-randomized trials: doubly robust estimation, efficiency considerations, and sensitivity analysis
• Cluster trials inference with CARE
• A causal framework for evaluating the total effect of strategies aiming to expand screening and to improve outcomes

This page was built for publication: Defining and estimating effects in cluster randomized trials: a methods comparison

Report a bug (only for logged in users!)Click here to report a bug for this page (MaRDI item Q6626873)