Uses and limitations of randomization-based efficacy estimators

DOI10.1191/0962280205SM406OAMaRDI QIDQ5424959zbMATH OpenOpenAlexWikidataFDO

Authors Ian R. White

Publication date 7 November 2007

Published in Statistical Methods in Medical Research (Search for Journal in Brave)

Full work available at URL https://doi.org/10.1191/0962280205sm406oa

Mathematics Subject Classification ID

Estimation in survival analysis and censored data (62N02) Applications of statistics to biology and medical sciences; meta analysis (62P10)

Recommendations

• Uses and limitations of randomization-based efficacy estimators
• Simple maximum likelihood estimates of efficacy in randomized trials and before-and-after studies, with implications for meta-analysis
• Simple maximum likelihood estimates of efficacy in randomized trials and before-and-after studies, with implications for meta-analysis
• A Comparison of Methods for Estimating the Causal Effect of a Treatment in Randomized Clinical Trials Subject to Noncompliance
• Randomization-based inference and the choice of randomization procedures

Cites work

• A causal proportional hazards estimator for the effect of treatment actually received in a randomized trial with all-or-nothing compliance
• A geometric approach to assess bias due to omitted covariates in generalized linear models
• Addressing complications of intention-to-treat analysis in the combined presence of all-or-none treatment-noncompliance and subsequent missing outcomes
• Assessing the effect of an influenza vaccine in an encouragement design
• Bayesian inference for causal effects in randomized experiments with noncompliance
• Correcting for non-compliance in randomized trials using rank preserving structural failure time models
• Correcting for non-compliance in randomized trials using structural nested mean models
• Correcting for Noncompliance and Dependent Censoring in an AIDS Clinical Trial with Inverse Probability of Censoring Weighted (IPCW) Log‐Rank Tests
• Estimating Outcome Distributions for Compliers in Instrumental Variables Models
• Principal stratification in causal inference
• Semiparametric instrumental variable estimation of treatment response models.
• Some Surprising Results about Covariate Adjustment in Logistic Regression Models

Cited in

(12)

• Instrumental variable estimation of early treatment effect in randomized screening trials
• A structural mean model to allow for noncompliance in a randomized trial comparing 2 active treatments
• Inference on treatment effects from a randomized clinical trial in the presence of premature treatment discontinuation: the SYNERGY trial
• Aberrant Effects of Treatment
• A Comparison of Methods for Estimating the Causal Effect of a Treatment in Randomized Clinical Trials Subject to Noncompliance
• Simple maximum likelihood estimates of efficacy in randomized trials and before-and-after studies, with implications for meta-analysis
• Why There's No Cause to Randomize
• Uses and limitations of randomization-based efficacy estimators
• Simple maximum likelihood estimates of efficacy in randomized trials and before-and-after studies, with implications for meta-analysis
• There Is Cause to Randomize
• Assessing the ratio of means as a causal estimand in clinical endpoint bioequivalence studies in the presence of intercurrent events
• Intention-to-treat analysis with treatment discontinuation and missing data in clinical trials

Describes a project that uses

Uses Software

• stcomply
• Stata

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